Researchers at the University of Basel have developed a gene therapy that could potentially treat a rare and currently fatal ...
Researchers identified a molecular pathway that can limit muscle repair, a finding that may guide future muscular dystrophy treatments.
Durham-based Precision BioSciences, a gene-editing company, has received regulatory clearance to begin a clinical study of its potential treatment for Duchenne muscular dystrophy (DMD), a rare ...
– Success in ameliorating muscle weakness with a ketogenic diet containing medium-chain triglycerides – Reduction of fibrosis and increase muscle strength in DMD model rats (9 months old) on a ...
In this phase 1-2 randomized controlled trial involving adults with myotonic dystrophy type 1, del-desiran was well-tolerated in most patients 2. The treatment was also associated with decreased ...
Researchers at the University of Basel have developed a gene therapy that could potentially treat a rare and currently fatal muscle disease in ...
Satellos Bioscience Inc. (Nasdaq: MSLE, TSX: MSCL) (“Satellos” or the “Company”), a clinical-stage biotechnology company developing life-improving medicines to treat degenerative muscle diseases, ...
On March 10, 2026, from 12:00 p.m. -- 1:30 p.m. ET, in room Key West ABCD at the Hilton Orlando, Avidity will host an industry forum lunch titled "Biomarker Advancements in Rare Neuromuscular Disease: ...
Long-term treatment with givinostat in boys with Duchenne muscular dystrophy continues to show a favourable safety and tolerability profile MILAN, Italy, October 07, 2025 – Italfarmaco S.p.A.
Satellos Bioscience Inc. (NASDAQ: MSLE, TSX: MSCL) (“Satellos” or the “Company”), a clinical-stage biotechnology company developing life-improving medicines to treat degenerative muscle diseases, ...